Suitability and readiness assessment of organizational resources for the implementation of gene therapy in hemophilia in Spain and Portugal: A survey-based study
Jose Manuel Calvo Villas a), Manuel Rodríguez López b), Jorge Cuesta Tovar c), Santiago Bonanad Boix d), Juan Carlos Reverter Calatayud e), María Teresa Álvarez-Román f)
a) Hematology Department, Hospital Universitario Miguel Servet, C/ Padre Arrupe s/n, 50009 Zaragoza, Spain
b) Hematology Department, Hospital Álvaro Cunqueiro, Estrada de Clara Campoamor, 341, 36312 Vigo, Spain
c) Hematology Department, Hospital Universitario de Toledo, Avenida Río Guadiana s/n, 45007 Toledo, Spain
d) Hematology Department, Hospital Universitari i Politècnic La Fe, Avinguda de Fernando Abril Martorell, 106, 46026 Valencia, Spain
e) Hemotherapy and Hemostasis Department, Hospital Clínic de Barcelona, Carrer de Villarroel, 170, 08036 Barcelona, Spain
f) Hematology Department, Hospital Universitario La Paz-IdiPaz, Universidad Autónoma de Madrid, Paseo de la Castellana, 261, 28046 Madrid, Spain
Highlights
• First study in Spain and Portugal to explore resources for gene therapy in PwH.
• High interest (83 %) among hematologists in administering gene therapy to PwH.
• The results support a Hub-and-spoke model for gene therapy implementation.
• There is a need for appropriate training and education of professionals and patients.
• Ongoing evaluation of infrastructure and resources is essential.